Hemophilia cure
At this time, there is no cure for hemophilia, but waiting for the results of gene therapy techniques.
Gene therapy for hemophilia is still under experiments. The idea of gene therapy is to use genes or genetic elements to manage or prevent disease. In general, gene therapy involves taking healthy genes (the ones that direct the body to produce clotting factor) and inserting them into the body of a patient with hemophilia. The new genes should increase the clotting factor level in the blood. Successful gene therapy eliminates the need for factor replacement. It cures hemophilia, but the gene may provide a partial cure. Gene therapy may reduce symptoms of severe hemophilia to a mild or moderate form. It is not currently an accepted therapy for hemophilia until now.
Liver transplants may help a small number of people with hemophilia to cure because the liver makes the clotting factor. The new livers they received made adequate amounts of the factor for them. Transplants are extremely dangerous to use as a cure for hemophilia. We do liver transplants only to save someone’s life when the liver has stopped working.
